[go: up one dir, main page]

SG11201701245QA - Methods for increasing cas9-mediated engineering efficiency - Google Patents

Methods for increasing cas9-mediated engineering efficiency

Info

Publication number
SG11201701245QA
SG11201701245QA SG11201701245QA SG11201701245QA SG11201701245QA SG 11201701245Q A SG11201701245Q A SG 11201701245QA SG 11201701245Q A SG11201701245Q A SG 11201701245QA SG 11201701245Q A SG11201701245Q A SG 11201701245QA SG 11201701245Q A SG11201701245Q A SG 11201701245QA
Authority
SG
Singapore
Prior art keywords
methods
engineering efficiency
mediated engineering
cas9
increasing
Prior art date
Application number
SG11201701245QA
Inventor
Peter Sean Cameron
Rachel E Haurwitz
Andrew P May
Christopher H Nye
Overbeek Megan Van
Original Assignee
Caribou Biosciences Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Caribou Biosciences Inc filed Critical Caribou Biosciences Inc
Publication of SG11201701245QA publication Critical patent/SG11201701245QA/en

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/11DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/87Introduction of foreign genetic material using processes not otherwise provided for, e.g. co-transformation
    • C12N15/90Stable introduction of foreign DNA into chromosome
    • C12N15/902Stable introduction of foreign DNA into chromosome using homologous recombination
    • C12N15/907Stable introduction of foreign DNA into chromosome using homologous recombination in mammalian cells
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/10Processes for the isolation, preparation or purification of DNA or RNA
    • C12N15/102Mutagenizing nucleic acids
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/11DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/111General methods applicable to biologically active non-coding nucleic acids
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N9/00Enzymes; Proenzymes; Compositions thereof; Processes for preparing, activating, inhibiting, separating or purifying enzymes
    • C12N9/14Hydrolases (3)
    • C12N9/16Hydrolases (3) acting on ester bonds (3.1)
    • C12N9/22Ribonucleases [RNase]; Deoxyribonucleases [DNase]
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y301/00Hydrolases acting on ester bonds (3.1)
    • C12Y301/30Endoribonucleases active with either ribo- or deoxyribonucleic acids and producing 5'-phosphomonoesters (3.1.30)
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2310/00Structure or type of the nucleic acid
    • C12N2310/10Type of nucleic acid
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2310/00Structure or type of the nucleic acid
    • C12N2310/10Type of nucleic acid
    • C12N2310/20Type of nucleic acid involving clustered regularly interspaced short palindromic repeats [CRISPR]

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Genetics & Genomics (AREA)
  • Engineering & Computer Science (AREA)
  • Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Biomedical Technology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Zoology (AREA)
  • Wood Science & Technology (AREA)
  • Molecular Biology (AREA)
  • General Engineering & Computer Science (AREA)
  • Biotechnology (AREA)
  • General Health & Medical Sciences (AREA)
  • Biochemistry (AREA)
  • Microbiology (AREA)
  • Plant Pathology (AREA)
  • Biophysics (AREA)
  • Physics & Mathematics (AREA)
  • Medicinal Chemistry (AREA)
  • Crystallography & Structural Chemistry (AREA)
  • Mycology (AREA)
  • Cell Biology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Epidemiology (AREA)
  • Animal Behavior & Ethology (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Peptides Or Proteins (AREA)
  • Preparation Of Compounds By Using Micro-Organisms (AREA)
SG11201701245QA 2014-08-27 2015-08-26 Methods for increasing cas9-mediated engineering efficiency SG11201701245QA (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201462042358P 2014-08-27 2014-08-27
US201462047495P 2014-09-08 2014-09-08
PCT/US2015/047046 WO2016033246A1 (en) 2014-08-27 2015-08-26 Methods for increasing cas9-mediated engineering efficiency

Publications (1)

Publication Number Publication Date
SG11201701245QA true SG11201701245QA (en) 2017-03-30

Family

ID=54140655

Family Applications (1)

Application Number Title Priority Date Filing Date
SG11201701245QA SG11201701245QA (en) 2014-08-27 2015-08-26 Methods for increasing cas9-mediated engineering efficiency

Country Status (11)

Country Link
US (2) US9970030B2 (en)
EP (1) EP3186376B1 (en)
AU (1) AU2015308910B2 (en)
CA (1) CA2959070C (en)
DK (1) DK3186376T3 (en)
ES (1) ES2730378T3 (en)
GB (1) GB2544001A (en)
IL (1) IL250700B (en)
NZ (1) NZ728437A (en)
SG (1) SG11201701245QA (en)
WO (1) WO2016033246A1 (en)

Families Citing this family (73)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US10323236B2 (en) 2011-07-22 2019-06-18 President And Fellows Of Harvard College Evaluation and improvement of nuclease cleavage specificity
HRP20181648T1 (en) 2013-04-16 2019-01-25 Regeneron Pharmaceuticals, Inc. TARGET GENOMIC TARGET MODIFICATION
US9163284B2 (en) 2013-08-09 2015-10-20 President And Fellows Of Harvard College Methods for identifying a target site of a Cas9 nuclease
US9359599B2 (en) 2013-08-22 2016-06-07 President And Fellows Of Harvard College Engineered transcription activator-like effector (TALE) domains and uses thereof
US9322037B2 (en) 2013-09-06 2016-04-26 President And Fellows Of Harvard College Cas9-FokI fusion proteins and uses thereof
US9340799B2 (en) 2013-09-06 2016-05-17 President And Fellows Of Harvard College MRNA-sensing switchable gRNAs
US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
MX388127B (en) 2013-12-11 2025-03-19 Regeneron Pharma METHODS AND COMPOSITIONS FOR THE TARGETED MODIFICATION OF A GENOME.
US20150165054A1 (en) 2013-12-12 2015-06-18 President And Fellows Of Harvard College Methods for correcting caspase-9 point mutations
US10077453B2 (en) 2014-07-30 2018-09-18 President And Fellows Of Harvard College CAS9 proteins including ligand-dependent inteins
ES2731437T3 (en) 2014-11-21 2019-11-15 Regeneron Pharma Methods and compositions for directed genetic modification through the use of guide RNA pairs
KR102763527B1 (en) 2014-12-03 2025-02-05 애질런트 테크놀로지스, 인크. Guide rna with chemical modifications
US12359197B2 (en) 2014-12-12 2025-07-15 Etagen Pharma, Inc. Compositions and methods for editing nucleic acids in cells utilizing oligonucleotides
ES2884838T3 (en) 2015-04-06 2021-12-13 Univ Leland Stanford Junior Chemically modified guide RNA for CRISPR / CAS-mediated gene regulation
US10167457B2 (en) 2015-10-23 2019-01-01 President And Fellows Of Harvard College Nucleobase editors and uses thereof
US11905521B2 (en) * 2015-11-17 2024-02-20 The Chinese University Of Hong Kong Methods and systems for targeted gene manipulation
EP3420080B1 (en) * 2016-02-22 2019-08-21 Caribou Biosciences, Inc. Methods for modulating dna repair outcomes
WO2017155408A1 (en) * 2016-03-11 2017-09-14 Erasmus University Medical Center Rotterdam Improved crispr-cas9 genome editing tool
EP3219799A1 (en) 2016-03-17 2017-09-20 IMBA-Institut für Molekulare Biotechnologie GmbH Conditional crispr sgrna expression
EP4495235A3 (en) * 2016-04-13 2025-05-21 Editas Medicine, Inc. Grna fusion molecules, gene editing systems, and methods of use thereof
EP3452055A4 (en) * 2016-05-06 2019-11-06 Tod M. Woolf IMPROVED METHODS OF GENOME EDITING WITH AND WITHOUT PROGRAMMABLE NUCLEASES
CN113831407B (en) 2016-05-20 2024-06-11 瑞泽恩制药公司 Methods for breaking immune tolerance using multiple guide RNAs
GB2582731B8 (en) * 2016-06-02 2021-10-27 Sigma Aldrich Co Llc Using programmable DNA binding proteins to enhance targeted genome modification
US10767175B2 (en) 2016-06-08 2020-09-08 Agilent Technologies, Inc. High specificity genome editing using chemically modified guide RNAs
WO2017214632A2 (en) * 2016-06-10 2017-12-14 University Of Wyoming Recombinant insect vectors and methods of use
JP6855037B2 (en) * 2016-07-19 2021-04-07 国立大学法人大阪大学 Genome editing method
KR20250103795A (en) 2016-08-03 2025-07-07 프레지던트 앤드 펠로우즈 오브 하바드 칼리지 Adenosine nucleobase editors and uses thereof
EP3497214B1 (en) 2016-08-09 2023-06-28 President and Fellows of Harvard College Programmable cas9-recombinase fusion proteins and uses thereof
US11466283B2 (en) 2016-08-18 2022-10-11 Canopy Growth Corporation Plants and methods for increasing and decreasing synthesis of cannabinoids
WO2018039438A1 (en) 2016-08-24 2018-03-01 President And Fellows Of Harvard College Incorporation of unnatural amino acids into proteins using base editing
AU2017342543B2 (en) 2016-10-14 2024-06-27 President And Fellows Of Harvard College AAV delivery of nucleobase editors
US10745677B2 (en) 2016-12-23 2020-08-18 President And Fellows Of Harvard College Editing of CCR5 receptor gene to protect against HIV infection
WO2018129368A2 (en) 2017-01-06 2018-07-12 Editas Medicine, Inc. Methods of assessing nuclease cleavage
US12390514B2 (en) 2017-03-09 2025-08-19 President And Fellows Of Harvard College Cancer vaccine
EP3592853A1 (en) 2017-03-09 2020-01-15 President and Fellows of Harvard College Suppression of pain by gene editing
US11542496B2 (en) 2017-03-10 2023-01-03 President And Fellows Of Harvard College Cytosine to guanine base editor
WO2018170015A1 (en) * 2017-03-14 2018-09-20 The Regents Of The University Of California Engineering crispr cas9 immune stealth
BR112019019655A2 (en) 2017-03-23 2020-04-22 Harvard College nucleobase editors comprising nucleic acid programmable dna binding proteins
US11680262B2 (en) * 2017-03-30 2023-06-20 Kyoto University Method for inducing exon skipping by genome editing
US12173309B2 (en) * 2017-04-10 2024-12-24 Max-Planck-Gesellschaft Zur Forderung Der Wissenschaften E.V. Compounds for increasing genome editing efficiency
WO2018209320A1 (en) 2017-05-12 2018-11-15 President And Fellows Of Harvard College Aptazyme-embedded guide rnas for use with crispr-cas9 in genome editing and transcriptional activation
US11732274B2 (en) 2017-07-28 2023-08-22 President And Fellows Of Harvard College Methods and compositions for evolving base editors using phage-assisted continuous evolution (PACE)
US11319532B2 (en) 2017-08-30 2022-05-03 President And Fellows Of Harvard College High efficiency base editors comprising Gam
CN111315889A (en) * 2017-09-08 2020-06-19 生命技术公司 Methods and compositions for enhancing homologous recombination
AU2018352592C1 (en) 2017-10-16 2025-09-25 Beam Therapeutics, Inc. Uses of adenosine base editors
CN111448313A (en) * 2017-11-16 2020-07-24 阿斯利康(瑞典)有限公司 Compositions and methods for improving the effectiveness of Cas9-based knock-in strategies
WO2019099982A1 (en) * 2017-11-17 2019-05-23 The Johns Hopkins University Compositions and methods for efficient genome editing
US12406749B2 (en) 2017-12-15 2025-09-02 The Broad Institute, Inc. Systems and methods for predicting repair outcomes in genetic engineering
WO2019222545A1 (en) 2018-05-16 2019-11-21 Synthego Corporation Methods and systems for guide rna design and use
US12157760B2 (en) 2018-05-23 2024-12-03 The Broad Institute, Inc. Base editors and uses thereof
US12522807B2 (en) 2018-07-09 2026-01-13 The Broad Institute, Inc. RNA programmable epigenetic RNA modifiers and uses thereof
ES3023563T3 (en) 2018-10-16 2025-06-02 Blueallele Corp Methods for targeted insertion of dna in genes
WO2020092453A1 (en) 2018-10-29 2020-05-07 The Broad Institute, Inc. Nucleobase editors comprising geocas9 and uses thereof
US12351837B2 (en) 2019-01-23 2025-07-08 The Broad Institute, Inc. Supernegatively charged proteins and uses thereof
CN114127285B (en) 2019-03-19 2024-09-10 布罗德研究所股份有限公司 Methods and compositions for editing nucleotide sequences
EP3956349A1 (en) 2019-04-17 2022-02-23 The Broad Institute, Inc. Adenine base editors with reduced off-target effects
WO2020243365A1 (en) * 2019-05-29 2020-12-03 Monsanto Technology Llc Directed genome engineering using enhanced targeted editing technologies
US12435330B2 (en) 2019-10-10 2025-10-07 The Broad Institute, Inc. Methods and compositions for prime editing RNA
DE112021002672T5 (en) 2020-05-08 2023-04-13 President And Fellows Of Harvard College METHODS AND COMPOSITIONS FOR EDIT BOTH STRANDS SIMULTANEOUSLY OF A DOUBLE STRANDED NUCLEOTIDE TARGET SEQUENCE
GB202007943D0 (en) * 2020-05-27 2020-07-08 Snipr Biome Aps Products & methods
WO2022060707A1 (en) * 2020-09-15 2022-03-24 Rutgers, The State University Of New Jersey Systems for gene editing and methods of use thereof
AU2022216614A1 (en) 2021-02-05 2023-02-23 Christiana Care Gene Editing Institute, Inc. Methods of and compositions for reducing gene expression and/or activity
US20220325338A1 (en) * 2021-04-02 2022-10-13 The Regents Of The University Of California Systems and methods for performing and measuring homologous chromosome template repair
WO2022256448A2 (en) * 2021-06-01 2022-12-08 Artisan Development Labs, Inc. Compositions and methods for targeting, editing, or modifying genes
CN115466780B (en) * 2021-06-10 2025-08-15 北京大学 Method for researching conformational change of Cas9 protein when recognizing target gene locus
US11884915B2 (en) 2021-09-10 2024-01-30 Agilent Technologies, Inc. Guide RNAs with chemical modification for prime editing
CN113801852B (en) * 2021-10-18 2023-08-18 齐齐哈尔医学院 A GPD1L-deleted human embryonic stem cell line and its construction method and application
EP4473108A1 (en) * 2022-02-02 2024-12-11 Biotalys NV Methods for genome editing
CN114703174B (en) * 2022-04-12 2023-10-24 中国科学院海洋研究所 CRISPR/Cas9 gene knockout method for rapidly obtaining genotype and phenotype mutation and application thereof
CN120077129A (en) * 2022-10-21 2025-05-30 沃奇酶科基因组学公司 Methods and compositions for sequencing library normalization
WO2024092217A1 (en) * 2022-10-27 2024-05-02 The Trustees Of Columbia University In The City Of New York Systems and methods for gene insertions
CN116286975A (en) * 2023-02-21 2023-06-23 浙江大学 A dCas9-based c-NHEJ fixed-site inhibition system and its application
CN117126828A (en) * 2023-09-15 2023-11-28 通用生物(安徽)股份有限公司 Method for improving in-vitro enzyme digestion efficiency of Cas9

Family Cites Families (55)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1152058A1 (en) * 2000-05-03 2001-11-07 Institut Curie Methods and compositions for effecting homologous recombination
US10087431B2 (en) 2010-03-10 2018-10-02 The Regents Of The University Of California Methods of generating nucleic acid fragments
BR112012028805A2 (en) 2010-05-10 2019-09-24 The Regents Of The Univ Of California E Nereus Pharmaceuticals Inc endoribonuclease compositions and methods of use thereof.
WO2013049330A1 (en) 2011-09-28 2013-04-04 The Regents Of The University Of California Synthetic transcriptional control elements and methods of generating and using such elements
US9895451B2 (en) 2011-12-02 2018-02-20 Yale University Formulations for targeted release of agents to low pH tissue environments or cellular compartments and methods of use thereof
GB201122458D0 (en) 2011-12-30 2012-02-08 Univ Wageningen Modified cascade ribonucleoproteins and uses thereof
WO2013122816A1 (en) 2012-02-13 2013-08-22 The Regents Of The University Of California Methods for genome-wide screening and construction of genetic interaction maps
RU2639277C2 (en) 2012-02-29 2017-12-20 Сангамо Байосайенсиз, Инк. Methods and compositions for huntington disease treatment
CN104364394B (en) 2012-03-17 2019-02-22 加州大学评议会 Rapid diagnosis and individualized treatment of acne
US9637739B2 (en) 2012-03-20 2017-05-02 Vilnius University RNA-directed DNA cleavage by the Cas9-crRNA complex
WO2013141680A1 (en) 2012-03-20 2013-09-26 Vilnius University RNA-DIRECTED DNA CLEAVAGE BY THE Cas9-crRNA COMPLEX
PT3241902T (en) 2012-05-25 2018-05-28 Univ California METHODS AND COMPOSITIONS FOR MODIFICATION OF TARGETED TARGET DNA BY RNA AND FOR MODULATION DIRECTED BY TRANSCRIPTION RNA
WO2013188638A2 (en) 2012-06-15 2013-12-19 The Regents Of The University Of California Endoribonucleases and methods of use thereof
KR102530118B1 (en) 2012-07-25 2023-05-08 더 브로드 인스티튜트, 인코퍼레이티드 Inducible dna binding proteins and genome perturbation tools and applications thereof
WO2014022702A2 (en) 2012-08-03 2014-02-06 The Regents Of The University Of California Methods and compositions for controlling gene expression by rna processing
CA2882499C (en) 2012-08-29 2023-09-26 Sangamo Biosciences, Inc. Cells genetically modified within the bcl11a gene by a nuclease and various aspects related thereto
UA118090C2 (en) 2012-09-07 2018-11-26 ДАУ АГРОСАЙЄНСІЗ ЕлЕлСі Fad2 performance loci and corresponding target site specific binding proteins capable of inducing targeted breaks
WO2014065596A1 (en) * 2012-10-23 2014-05-01 Toolgen Incorporated Composition for cleaving a target dna comprising a guide rna specific for the target dna and cas protein-encoding nucleic acid or cas protein, and use thereof
CA2890160A1 (en) 2012-10-31 2014-05-08 Cellectis Coupling herbicide resistance with targeted insertion of transgenes in plants
US10272163B2 (en) 2012-12-07 2019-04-30 The Regents Of The University Of California Factor VIII mutation repair and tolerance induction
WO2014093694A1 (en) 2012-12-12 2014-06-19 The Broad Institute, Inc. Crispr-cas nickase systems, methods and compositions for sequence manipulation in eukaryotes
ES2553782T3 (en) 2012-12-12 2015-12-11 The Broad Institute, Inc. Systems engineering, methods and guide compositions optimized for sequence manipulation
KR20150105634A (en) 2012-12-12 2015-09-17 더 브로드 인스티튜트, 인코퍼레이티드 Engineering and optimization of improved systems, methods and enzyme compositions for sequence manipulation
EP2931899A1 (en) 2012-12-12 2015-10-21 The Broad Institute, Inc. Functional genomics using crispr-cas systems, compositions, methods, knock out libraries and applications thereof
DK2784162T3 (en) 2012-12-12 2015-07-13 Broad Inst Inc Design of systems, methods and optimized control manipulations for sequence manipulation
EP4234696A3 (en) 2012-12-12 2023-09-06 The Broad Institute Inc. Crispr-cas component systems, methods and compositions for sequence manipulation
SG10201707569YA (en) 2012-12-12 2017-10-30 Broad Inst Inc Delivery, Engineering and Optimization of Systems, Methods and Compositions for Sequence Manipulation and Therapeutic Applications
US8697359B1 (en) 2012-12-12 2014-04-15 The Broad Institute, Inc. CRISPR-Cas systems and methods for altering expression of gene products
WO2014093655A2 (en) 2012-12-12 2014-06-19 The Broad Institute, Inc. Engineering and optimization of systems, methods and compositions for sequence manipulation with functional domains
DK3553174T3 (en) * 2012-12-17 2025-08-04 Harvard College RNA-GUIDED MODIFICATION OF THE HUMAN GENOME
US10513698B2 (en) 2012-12-21 2019-12-24 Cellectis Potatoes with reduced cold-induced sweetening
CN103981147B (en) 2013-02-08 2017-11-10 中国科学院上海生命科学研究院 A kind of new method for preparing hepatic parenchymal cells
US20140288421A1 (en) 2013-03-12 2014-09-25 The Regents Of The University Of California Gas vesicle ultrasound contrast agents and methods of using the same
US20140288411A1 (en) 2013-03-12 2014-09-25 The Regents Of The University Of California Gas vesicle magnetic resonance imaging contrast agents and methods of using the same
NZ712727A (en) 2013-03-14 2017-05-26 Caribou Biosciences Inc Compositions and methods of nucleic acid-targeting nucleic acids
US11332719B2 (en) 2013-03-15 2022-05-17 The Broad Institute, Inc. Recombinant virus and preparations thereof
AU2014235968B2 (en) 2013-03-21 2018-05-24 Ospedale San Raffaele Srl Targeted disruption of T cell receptor genes using engineered zinc finger protein nucleases
CN115261411A (en) 2013-04-04 2022-11-01 哈佛学院校长同事会 Therapeutic uses of genome editing with CRISPR/Cas systems
US9902973B2 (en) 2013-04-11 2018-02-27 Caribou Biosciences, Inc. Methods of modifying a target nucleic acid with an argonaute
CA2910489A1 (en) 2013-05-15 2014-11-20 Sangamo Biosciences, Inc. Methods and compositions for treatment of a genetic condition
US20140349405A1 (en) 2013-05-22 2014-11-27 Wisconsin Alumni Research Foundation Rna-directed dna cleavage and gene editing by cas9 enzyme from neisseria meningitidis
WO2014191518A1 (en) 2013-05-29 2014-12-04 Cellectis A method for producing precise dna cleavage using cas9 nickase activity
MX385330B (en) 2013-06-04 2025-03-18 Harvard College RIBONUCLEIC ACID-GUIDED TRANSCRIPTIONAL REGULATION.
US9267135B2 (en) 2013-06-04 2016-02-23 President And Fellows Of Harvard College RNA-guided transcriptional regulation
WO2015031619A1 (en) 2013-08-28 2015-03-05 Sangamo Biosciences, Inc. Compositions for linking dna-binding domains and cleavage domains
US20160298096A1 (en) 2013-11-18 2016-10-13 Crispr Therapeutics Ag Crispr-cas system materials and methods
AU2014363991B2 (en) 2013-12-09 2020-08-27 Sangamo Therapeutics, Inc. Methods and compositions for genome engineering
JP2017501149A (en) 2013-12-12 2017-01-12 ザ・ブロード・インスティテュート・インコーポレイテッド Delivery, use and therapeutic applications of CRISPR-CAS systems and compositions for targeting disorders and diseases using particle delivery components
US20150191744A1 (en) 2013-12-17 2015-07-09 University Of Massachusetts Cas9 effector-mediated regulation of transcription, differentiation and gene editing/labeling
US10774338B2 (en) 2014-01-16 2020-09-15 The Regents Of The University Of California Generation of heritable chimeric plant traits
DK3102673T3 (en) 2014-02-03 2020-07-06 Sangamo Therapeutics Inc METHODS AND COMPOSITIONS FOR THE TREATMENT OF BETA-TALASSEMI
WO2015143046A2 (en) 2014-03-18 2015-09-24 Sangamo Biosciences, Inc. Methods and compositions for regulation of zinc finger protein expression
WO2015171932A1 (en) 2014-05-08 2015-11-12 Sangamo Biosciences, Inc. Methods and compositions for treating huntington's disease
US9944933B2 (en) * 2014-07-17 2018-04-17 Georgia Tech Research Corporation Aptamer-guided gene targeting
IL287561B2 (en) * 2014-10-01 2024-03-01 Massachusetts Gen Hospital Methods for increasing the efficiency of nuclease-induced homology-directed repair

Also Published As

Publication number Publication date
AU2015308910B2 (en) 2017-12-07
GB2544001A (en) 2017-05-03
IL250700B (en) 2020-10-29
US20160257973A1 (en) 2016-09-08
GB201703026D0 (en) 2017-04-12
EP3186376B1 (en) 2019-03-20
US9970030B2 (en) 2018-05-15
NZ728437A (en) 2018-02-23
EP3186376A1 (en) 2017-07-05
DK3186376T3 (en) 2019-05-06
US20180171360A1 (en) 2018-06-21
AU2015308910A1 (en) 2017-02-09
WO2016033246A1 (en) 2016-03-03
ES2730378T3 (en) 2019-11-11
CA2959070A1 (en) 2016-03-03
CA2959070C (en) 2020-11-10
IL250700A0 (en) 2017-04-30

Similar Documents

Publication Publication Date Title
IL250700A0 (en) Methods for increasing cas9-mediated engineering efficiency
GB201406151D0 (en) Method
GB201409558D0 (en) Method
GB201406155D0 (en) Method
GB201408119D0 (en) Method
GB201413240D0 (en) Method
GB201414496D0 (en) Method
GB201403470D0 (en) Method
GB201410022D0 (en) Method
GB201410101D0 (en) Method
GB201412802D0 (en) Method
GB201411500D0 (en) Method
GB201416849D0 (en) Method
GB201416675D0 (en) Method
GB201409234D0 (en) Method
GB201409128D0 (en) Method
GB201414181D0 (en) Method
GB201412736D0 (en) Method
GB201412226D0 (en) Method
GB201409101D0 (en) Method
GB201413929D0 (en) Method
GB201413612D0 (en) Method
GB201408649D0 (en) Method
GB201407971D0 (en) Method
GB201409206D0 (en) Block turbine