Safety of AAV factor IX peripheral transvenular gene delivery to muscle in hemophilia B dogs. (Q34025098)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

title

Safety of AAV factor IX peripheral transvenular gene delivery to muscle in hemophilia B dogs (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

main subject

hemophilia

0 references

coagulation factor IX

0 references

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

Federico Mingozzi

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

George Buchlis

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

Daniel J Hui

1 reference

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1 February 2020

Yifeng Chen

1 reference

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1 February 2020

Etiena Basner-Tschakarjan

1 reference

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1 February 2020

Valder R Arruda

1 reference

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1 February 2020

Antoneta Radu

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

Helen G Franck

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

J Fraser Wright

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

Shangzhen Zhou

1 reference

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1 February 2020

Hansell H Stedman

1 reference

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1 February 2020

Dwight A Bellinger

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

Timothy C Nichols

1 reference

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1 February 2020

publication date

27 April 2010

1 reference

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1 February 2020

1 reference

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1 February 2020

volume

1 reference

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1 February 2020

issue

1 reference

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1 February 2020

page(s)

1318-1329

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

Safety and efficacy of subretinal readministration of a viral vector in large animals to treat congenital blindness

1 February 2020

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Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.

5 July 2018

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Impact of the underlying mutation and the route of vector administration on immune responses to factor IX in gene therapy for hemophilia B.

5 July 2018

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5 July 2018

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5 July 2018

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When to treat and the benefits of treating hepatitis C in patients with haemophilia

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Reversal of blindness in animal models of leber congenital amaurosis using optimized AAV2-mediated gene transfer

5 July 2018

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5 July 2018

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A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

5 July 2018

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Results and harmonization guidelines from two large-scale international Elispot proficiency panels conducted by the Cancer Vaccine Consortium (CVC/SVI)

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model

5 July 2018

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5 July 2018

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Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1.

5 July 2018

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5 July 2018

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AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

5 July 2018

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5 July 2018

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Gene therapy for hemophilia B: AAV-mediated transfer of the gene for coagulation factor IX to human muscle.

5 July 2018

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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

5 July 2018

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Canine hemophilia B resulting from a point mutation with unusual consequences

5 July 2018

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Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins

5 July 2018

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Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients

29 October 2018

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29 October 2018

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Efficient induction of immune tolerance to coagulation factor IX following direct intramuscular gene transfer

29 October 2018

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Immunity to adeno-associated virus-mediated gene transfer in a random-bred canine model of Duchenne muscular dystrophy

29 October 2018

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Uniform scale-independent gene transfer to striated muscle after transvenular extravasation of vector

29 October 2018

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Major role of local immune responses in antibody formation to factor IX in AAV gene transfer

29 October 2018

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29 October 2018

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Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice

29 October 2018

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Influence of vector dose on factor IX-specific T and B cell responses in muscle-directed gene therapy

29 October 2018

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Muscle-directed gene transfer and transient immune suppression result in sustained partial correction of canine hemophilia B caused by a null mutation

29 October 2018

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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

29 October 2018

1 reference

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Cyclic stretch upregulates production of interleukin-8 and monocyte chemotactic and activating factor/monocyte chemoattractant protein-1 in human endothelial cells

29 October 2018

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Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver

29 October 2018

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Inhibition of human natural cytotoxicity by macromolecular antiproteases

29 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20424599

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Anti-thymocyte globulin (ATG) prevents autoimmune encephalomyelitis by expanding myelin antigen-specific Foxp3+ regulatory T cells

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20424599

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Safety and Efficacy of Regional Intravenous (RI) Versus Intramuscular (IM) Delivery of rAAV1 and rAAV8 to Nonhuman Primate Skeletal Muscle.

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FMT.2010.73

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/MT.2010.73

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json

1 February 2020

PubMed publication ID

20424599

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20424599%20AND%20SRC:MED&resulttype=core&format=json