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Alateeq, 2016 - Google Patents

CRISPR/Cas9-mediated traceless gene correction and activation of the HBB locus in iPSCs with the beta thalassaemia mutation

Alateeq, 2016

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Document ID
9423812088202535371
Author
Alateeq S
Publication year

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Beta thalassaemia is caused by mutations in the adult haemoglobin gene (HBB) and is one of the most prevalent monogenic blood disorders worldwide. The transplantation of haematopoietic stem cells derived from gene-corrected patient induced pluripotent stem …
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