(Q28115950)

4 January 2017

title

Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer (English)

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4 January 2017

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J. H. Wolfe

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4 January 2017

M. S. Sands

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4 January 2017

J. E. Barker

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4 January 2017

B. Gwynn

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4 January 2017

L. B. Rowe

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4 January 2017

C. A. Vogler

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4 January 2017

E. H. Birkenmeier

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4 January 2017

language of work or name

English

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publication date

24 December 2016

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4 January 2017

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4 January 2017

volume

360

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4 January 2017

issue

6406

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4 January 2017

page(s)

749–753

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Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis

4 January 2017

cites work

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7 January 2021

Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency

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7 January 2021

Inborn errors of mucopolysaccharide metabolism

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7 January 2021

Restoration of normal lysosomal function in mucopolysaccharidosis type VII cells by retroviral vector-mediated gene transfer

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7 January 2021

Progress toward human gene therapy

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7 January 2021

Human gene therapy comes of age.

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7 January 2021

Beta-glucuronidase mediated pathway essential for retinal pigment epithelial degradation of glycosaminoglycans. Disease expression and in vitro disease correction using retroviral mediated cDNA transfer

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7 January 2021

Genes transferred by retroviral vectors into normal and mutant myoblasts in primary cultures are expressed in myotubes

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7 January 2021

Herpesvirus vector gene transfer and expression of beta-glucuronidase in the central nervous system of MPS VII mice

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7 January 2021

Clonal and systemic analysis of long-term hematopoiesis in the mouse.

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7 January 2021

Long-Term Improvement of Hypercholesterolemia After Ex Vivo Gene Therapy in LDLR-Deficient Rabbits

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7 January 2021

Site-directed neovessel formation in vivo

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7 January 2021

A safe packaging line for gene transfer: separating viral genes on two different plasmids

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7 January 2021

Combination of interleukins 3 and 6 preserves stem cell function in culture and enhances retrovirus-mediated gene transfer into hematopoietic stem cells

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7 January 2021

Nucleotide sequence of rat preputial gland beta-glucuronidase cDNA and in vitro insertion of its encoded polypeptide into microsomal membranes

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7 January 2021

Dimensions Publication ID

Identifiers

DOI

10.1038/360749A0

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1020719652

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